[논문] Advancing gene therapy for phenylketonuria: From precision editing to clinical translation
[논문] Modeling fabry disease-associated cardiovascular phenotypes using isogenic α-Galactosidase A-knockout human induced pluripotent stem cells
[논문] High-efficiency base editing for nuclear and mitochondrial DNA with an optimized DYW-like deaminase
[논문] Antibacterial effect of phospholipid-based nanotube structures on protein nanoparticles via membrane disruption
[논문] Advances in the Rational Design of Ionizable Lipids For mRNA Therapeutics
[논문] Human Opsin Restoration by Histone Methylation using Methyltransferase Fusion Protein SETD7-dCas9
[논문] Engineered virus-like particles for in vivo gene editing ameliorate hearing loss in murine DFNA2 mode
[논문] Bystander editing by adenine base editors impairs vision restoration in a mouse model of Leber congenital amaurosis
[논문] Cas9-expressing cattle using the PiggyBac transposon all-in-one system
[논문] Transferrin-binding domain inserted-adenovirus hexon engineering enables systemic immune evasion and intratumoral T-cell activation
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